Japan’s cost-effectiveness assessment (CEA) panel has approved a revised handling policy for the CEA system for FY2026, with the health…
ACADEMIA
Exon 44-Targeted DMD Drug Hits Goals in PI/II: NCNP/Nippon Shinyaku
The National Center of Neurology and Psychiatry (NCNP) and Nippon Shinyaku said on March 17 that their investigational Duchenne muscular dystrophy (DMD) treatment NS-089/NCNP-02, the world’s first exon 44 skipping drug, showed promise in an investigator-led PI/II study. DMD is…
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