Japan is considering a new approach to its “special” market expansion re-pricing that would exclude drug sales tied to private…
BUSINESS
Nippon Shinyaku’s DMD Drug Gets Rare Pediatric Disease Tag in US
Nippon Shinyaku said on July 4 that the US FDA has awarded a rare pediatric disease designation to brogidirsen, the company’s antisense oligonucleotide therapy being developed for the treatment of Duchenne muscular dystrophy (DMD).Otherwise known as NS-089/NCNP-02, brogidirsen is an…
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