Japan’s Ministry of Health, Labor and Welfare (MHLW) on March 5 unveiled the revised NHI prices for drugs subject to…
BUSINESS
JCR’s Hurler Syndrome Drug Gets Orphan Status in US
JCR Pharmaceuticals said on February 12 that it has earned orphan drug designation for JR-171, a blood-brain-barrier (BBB)-penetrating α-L-iduronidase, for the treatment of mucopolysaccharidosis type 1 (Hurler, Hurler-Scheie, and Scheie syndrome).The company is running a PI/II trial globally for JR-171,…
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