Japan’s cost-effectiveness assessment (CEA) panel has approved a revised handling policy for the CEA system for FY2026, with the health…
BUSINESS
JCR’s Hurler Syndrome Drug Earns Fast-Track Status in US
JCR Pharmaceuticals said on October 5 that it has won the US FDA’s fast-track designation for JR-171, a blood-brain-barrier (BBB)-penetrating recombinant α-L-iduronidase, for the treatment of mucopolysaccharidosis (MPS) type 1 (Hurler, Hurler-Scheie, and Scheie syndrome). Developed using the company’s proprietary…
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