Japan’s cost-effectiveness assessment (CEA) panel has approved a revised handling policy for the CEA system for FY2026, with the health…
BUSINESS
Astellas’ Pompe Gene Therapy Trial Hit with FDA Clinical Hold
Astellas Pharma said on June 27 that the US FDA has placed a clinical hold on a PI/II trial for AT845, its investigational gene therapy for Pompe disease, after one study participant experienced a serious adverse event of peripheral sensory…
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