BUSINESS
Sephience Seen as Potential First-Line PKU Therapy: Professor
PTC Therapeutics Japan’s phenylketonuria (PKU) treatment Sephience (sepiapterin), launched earlier in the month, could emerge as a first-line option for the disorder, a specialist said, highlighting its potential to ease strict dietary restrictions for patients. Speaking at a media seminar…
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A few weeks ago, I had coffee with a very talented executive. Let’s call him Kenji. He has a great job, a big salary, and a solid team. But he was unhappy. He felt bored and wanted a new challenge.…





