Japan’s cost-effectiveness assessment (CEA) panel has approved a revised handling policy for the CEA system for FY2026, with the health…
BUSINESS
Regenxbio Clears Path to Resubmit Hunter Syndrome Gene Therapy
Regenxbio has reached an agreement with the US FDA on a path forward for resubmitting its application for Navsunli (clemidsogene lanparvovec), its Hunter syndrome gene therapy partnered with Nippon Shinyaku. The development marks a turnaround for the program, also known…
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