Japan is pressing ahead with broader drug price cuts under its cost-effectiveness assessment (CEA) system, despite lingering questions over the…
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Ultragenyx’s Gene Therapy in Line for Orphan Tag in Japan
A Japanese health ministry panel on September 20 agreed to grant orphan designation for Ultragenyx Japan’s gene therapy DTX401 (pariglasgene brecaparvovec) for the treatment of glycogen storage disease type Ia, or GSDIa. According to the company, GSDIa is caused by…
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