Eltrombopag, Nusinersen Designated as Orphan Drugs

November 28, 2016
The Ministry of Health, Labor and Welfare (MHLW) on November 24 granted orphan drug designation to two compounds - Novartis Pharma’s eltrombopag olamine and Biogen Japan’s nusinersen sodium. Eltrombopag olamine carries a proposed indication of aplastic anemia, while nusinersen is...read more