December 6, 2011
The Pharmaceutical Affairs and Food Sanitation Council’s (PAFSC) First Committee on New Drugs approved orphan drug designations for Novartis Pharma’s everolimus (expected indication: tuberous sclerosis complex (TSC)) and Pfizer Japan’s tafamidis meglumine (transthyretin amyloid polyneuropathy (TTR), also known as familial...read more