BUSINESS

Amicus’ Pompe Disease Drugs Hit Japan Market

August 28, 2025
Amicus Therapeutics said on August 27 that it has launched Pombiliti (cipaglucosidase alfa) and Opfolda (miglustat) in Japan as a two-component regimen for the treatment of late-onset Pompe disease. Late-onset Pompe disease is a lysosomal disorder caused by a deficiency…

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