August 22, 2019
The Ministry of Health, Labor and Welfare (MHLW) on August 20 granted orphan drug designation to Nippon Shinyaku’s antisense oligonucleotide viltolarsen for the treatment of Duchenne muscular dystrophy (DMD). Viltolarsen, formerly known as NS-065/NCNP-01, was granted the orphan status for...read more